2

Understanding off-label use and the new challenges

Year:
2014
Language:
english
File:
PDF, 261 KB
english, 2014
4

Rare diseases and orphan drugs: 500 years ago

Year:
2015
Language:
english
File:
PDF, 350 KB
english, 2015
6

Compounded medication for patients with rare diseases

Year:
2018
Language:
english
File:
PDF, 398 KB
english, 2018
10

Orphan Drugs for Rare Diseases: Grounds for Special Status

Year:
2012
Language:
english
File:
PDF, 76 KB
english, 2012
11

Orphan Drugs for Rare Diseases

Year:
2012
Language:
english
File:
PDF, 128 KB
english, 2012
12

Cost-Effectiveness Assessment of Orphan Drugs

Year:
2013
Language:
english
File:
PDF, 196 KB
english, 2013
16

An Asymptomatic Patient with Severe Airway Obstruction

Year:
2011
Language:
english
File:
PDF, 428 KB
english, 2011
22

From promising molecules to orphan drugs: Early clinical drug development

Year:
2017
Language:
english
File:
PDF, 356 KB
english, 2017